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3. Natural History Vs New History: Infantile Onset with Dr. Priya Kishnani
2. Natural History Vs New History with Treatment with Dr. Pascal Laforêt
2016 Rare Disease Hero in Lysosomal Disorders - Duke's Priya Kishnani
How Duke University Has Led Pompe Disease Research
The Benefits of Newborn Screening for Pompe Disease
Pompe Positive - What's Next? Part 4
WORLDSymposium™ 2022 - Avalglucosidase alfa Trial Data
Pompe Positive - What's Next? Part 1
How to Monitor LOPD Patients Diagnosed Through NBS
Pediatric Grand Rounds: Lessons Learned from Rare Diseases: Bench to Bedside and Back
1. Crash Course in Pompe with Dr. Arnold Reuser
Expanded Newborn Screening for Pompe Disease and Mucopolysaccharidosis Type 1 | UPMC Children's
